MEDizzy
MEDizzy
Sadia
Sadiaover 1 year ago
Treatment for Gangliosidosis GM1

Treatment for Gangliosidosis GM1

There are currently no disease-modifying treatments for GM1 gangliosidosis. The Lysogene clinical study is testing an investigational gene therapy that aims to insert a working GLB1 gene into the cells of the brain and spinal cord.

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